Mucopolysaccharidosis VII
Showing 1 - 25 of 245
Mucopolysaccharidosis I, Mucopolysaccharidosis II, Mucopolysaccharidosis IV A Trial in San Francisco (There is no intervention)
Recruiting
- Mucopolysaccharidosis I
- +7 more
- There is no intervention
-
San Francisco, CaliforniaUniversity of California San Francisco
Nov 9, 2022
MPS (RaDiCo Cohort) (RaDiCo-MPS)
Recruiting
- Mucopolysaccharidosis I
- +7 more
-
Angers, France
- +22 more
Sep 12, 2023
ScreenPlus: A Comprehensive, Flexible, Multi-disorder Newborn
Enrolling by invitation
- Acid Sphingomyelinase Deficiency
- +13 more
- Confirmatory Testing
-
Bronx, New York
- +9 more
May 9, 2022
Mucopolysaccharidosis Disorders, Hurler Syndrome, Hunter Syndrome Trial in Minneapolis (Stem Cell Transplantation, IMD
Recruiting
- Mucopolysaccharidosis Disorders
- +28 more
- Stem Cell Transplantation
- +7 more
-
Minneapolis, MinnesotaMasonic Cancer Center, University of Minnesota
Nov 1, 2022
Baby Detect : Genomic Newborn Screening
Recruiting
- Congenital Adrenal Hyperplasia
- +126 more
-
Liege, Wallonia, BelgiumCRMN, Hôpital La Citadelle
Jan 24, 2023
Biomarker for Sly Disease (MPS VII) (BioSly)
Active, not recruiting
- Developmental Delay
- +3 more
-
Cairo, Egypt
- +4 more
May 12, 2021
Brain Structure and Function in MPS Disorders
Completed
- Mucopolysaccharidosis Type I
- +4 more
-
Oakland, California
- +3 more
Sep 4, 2019
MPS I, MPS II, MPS IVA Trial in San Francisco (Aldurazyme (laronidase))
Recruiting
- MPS I
- +8 more
- Aldurazyme (laronidase)
-
San Francisco, CaliforniaUniversity of California
Apr 21, 2022
Hemophilia A, Hemophilia B Trial in China (Recombinant human activated coagulation factor VII for injection)
Recruiting
- Hemophilia A
- Hemophilia B
- Recombinant human activated coagulation factor VII for injection
-
Chongqing, Chongqing, China
- +8 more
Aug 2, 2022
Mucopolysaccharidosis IH/S, Mucopolysaccharidosis IS Trial in Minneapolis (Autologous Plasmablasts (B cells))
Not yet recruiting
- Mucopolysaccharidosis IH/S
- Mucopolysaccharidosis IS
- Autologous Plasmablasts (B cells)
-
Minneapolis, MinnesotaUniversity of Minnesota
Jan 20, 2023
Before and After Hematopoietic Cell Transplantation in
Enrolling by invitation
- Hematopoietic Cell Transplantation
- Mucopolysaccharidosis Type I
- Laronidase therapy and a stem cell transplant
-
Minneapolis, MinnesotaUniversity of Minnesota Masonic Cancer Center
Nov 22, 2022
Mucopolysaccharidosis Type II Observational
Withdrawn
- Mucopolysaccharidosis II
- Observational
-
Oakland, California
- +2 more
Oct 6, 2022
Mucopolysaccharidosis Type IIIB, MPS III B Trial in Worldwide (AX 250)
Active, not recruiting
- Mucopolysaccharidosis Type IIIB
- MPS III B
- AX 250
-
Oakland, California
- +7 more
Jan 16, 2023
Mucopolysaccharidosis I, Mucopolysaccharidosis II, Mucopolysaccharidosis VI Trial in Torrance (Adalimumab Injection [Humira],
Recruiting
- Mucopolysaccharidosis I
- +2 more
- Adalimumab Injection [Humira]
- Saline Solution for Injection
-
Torrance, CaliforniaThe Lundquist Institute at Harbor-UCLA Medical Center
Aug 9, 2022
Ophthalmic Manifestations of Patients With Mucopolysaccharidosis
Recruiting
- Ophthalmic Manifestations
-
Assiut, EgyptAssiut University
Feb 22, 2021
Fascial Versus Standard Neck Dissection in N1b Papillary Thyroid
Completed
- Patients With Papillary Thyroid Cancer and N1b Status
- Fascial Neck Dissection
- Standard Neck Dissection
-
Rome, ItalyFondazione Policlinico Universitario Agostino Gemelli IRCCS
Mar 27, 2023
Set for Head, Neck and Respiratory Disease in
Completed
- Mucopolysaccharidosis Type II
-
Manchester, Lancashire, United KingdomManchester University NHS Foundation Trust
Aug 31, 2023
Mucopolysaccharidosis Type II Natural History
Completed
- Mucopolysaccharidosis II
-
Pittsburgh, Pennsylvania
- +2 more
Apr 22, 2022