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Mucopolysaccharidosis VII

Showing 1 - 25 of 245

STUDY
CONDITIONS
INTERVENTIONS
LOCATIONS

MPS VII, Mucopolysaccharidosis VII, Sly Syndrome Trial (Mepsevii)

Available
  • MPS VII
  • +2 more
  • (no location specified)
Nov 22, 2022

Mucopolysaccharidosis I, Mucopolysaccharidosis II, Mucopolysaccharidosis IV A Trial in San Francisco (There is no intervention)

Recruiting
  • Mucopolysaccharidosis I
  • +7 more
  • There is no intervention
  • San Francisco, California
    University of California San Francisco
Nov 9, 2022

MPS (RaDiCo Cohort) (RaDiCo-MPS)

Recruiting
  • Mucopolysaccharidosis I
  • +7 more
    • Angers, France
    • +22 more
    Sep 12, 2023

    ScreenPlus: A Comprehensive, Flexible, Multi-disorder Newborn

    Enrolling by invitation
    • Acid Sphingomyelinase Deficiency
    • +13 more
    • Confirmatory Testing
    • Bronx, New York
    • +9 more
    May 9, 2022

    Mucopolysaccharidosis Disorders, Hurler Syndrome, Hunter Syndrome Trial in Minneapolis (Stem Cell Transplantation, IMD

    Recruiting
    • Mucopolysaccharidosis Disorders
    • +28 more
    • Stem Cell Transplantation
    • +7 more
    • Minneapolis, Minnesota
      Masonic Cancer Center, University of Minnesota
    Nov 1, 2022

    Baby Detect : Genomic Newborn Screening

    Recruiting
    • Congenital Adrenal Hyperplasia
    • +126 more
      • Liege, Wallonia, Belgium
        CRMN, Hôpital La Citadelle
      Jan 24, 2023

      Biomarker for Sly Disease (MPS VII) (BioSly)

      Active, not recruiting
      • Developmental Delay
      • +3 more
        • Cairo, Egypt
        • +4 more
        May 12, 2021

        Sly Syndrome, MPS VII, Mucopolysaccharidosis Trial in Worldwide (UX003)

        Completed
        • Sly Syndrome
        • +3 more
        • Oakland, California
        • +6 more
        Jul 16, 2020

        MPS 7, Sly Syndrome, Mucopolysaccharidosis Trial in United States (UX003, Placebo)

        Completed
        • MPS 7
        • +3 more
        • Oakland, California
        • +3 more
        Jul 16, 2020

        Brain Structure and Function in MPS Disorders

        Completed
        • Mucopolysaccharidosis Type I
        • +4 more
          • Oakland, California
          • +3 more
          Sep 4, 2019

          MPS I, MPS II, MPS IVA Trial in San Francisco (Aldurazyme (laronidase))

          Recruiting
          • MPS I
          • +8 more
          • Aldurazyme (laronidase)
          • San Francisco, California
            University of California
          Apr 21, 2022

          Hemophilia A, Hemophilia B Trial in China (Recombinant human activated coagulation factor VII for injection)

          Recruiting
          • Hemophilia A
          • Hemophilia B
          • Recombinant human activated coagulation factor VII for injection
          • Chongqing, Chongqing, China
          • +8 more
          Aug 2, 2022

          Mucopolysaccharidosis IH/S, Mucopolysaccharidosis IS Trial in Minneapolis (Autologous Plasmablasts (B cells))

          Not yet recruiting
          • Mucopolysaccharidosis IH/S
          • Mucopolysaccharidosis IS
          • Autologous Plasmablasts (B cells)
          • Minneapolis, Minnesota
            University of Minnesota
          Jan 20, 2023

          Before and After Hematopoietic Cell Transplantation in

          Enrolling by invitation
          • Hematopoietic Cell Transplantation
          • Mucopolysaccharidosis Type I
          • Laronidase therapy and a stem cell transplant
          • Minneapolis, Minnesota
            University of Minnesota Masonic Cancer Center
          Nov 22, 2022

          Mucopolysaccharidosis Type II Observational

          Withdrawn
          • Mucopolysaccharidosis II
          • Observational
          • Oakland, California
          • +2 more
          Oct 6, 2022

          Mucopolysaccharidosis I Trial in Brazil, Japan, United States (JR-171)

          Completed
          • Mucopolysaccharidosis I
          • Oakland, California
          • +5 more
          Aug 16, 2022

          Mucopolysaccharidosis II Trial in Japan (JR-141)

          Completed
          • Mucopolysaccharidosis II
          • Gifu, Japan
          • +7 more
          Nov 10, 2022

          Mucopolysaccharidosis II Trial in Oakland, Chapel Hill (DNL310, Idursulfase)

          Recruiting
          • Mucopolysaccharidosis II
          • Oakland, California
          • +11 more
          Jan 9, 2023

          Mucopolysaccharidosis Type IIIB, MPS III B Trial in Worldwide (AX 250)

          Active, not recruiting
          • Mucopolysaccharidosis Type IIIB
          • MPS III B
          • AX 250
          • Oakland, California
          • +7 more
          Jan 16, 2023

          Mucopolysaccharidosis I, Mucopolysaccharidosis II, Mucopolysaccharidosis VI Trial in Torrance (Adalimumab Injection [Humira],

          Recruiting
          • Mucopolysaccharidosis I
          • +2 more
          • Adalimumab Injection [Humira]
          • Saline Solution for Injection
          • Torrance, California
            The Lundquist Institute at Harbor-UCLA Medical Center
          Aug 9, 2022

          Ophthalmic Manifestations of Patients With Mucopolysaccharidosis

          Recruiting
          • Ophthalmic Manifestations
            • Assiut, Egypt
              Assiut University
            Feb 22, 2021

            Fascial Versus Standard Neck Dissection in N1b Papillary Thyroid

            Completed
            • Patients With Papillary Thyroid Cancer and N1b Status
            • Fascial Neck Dissection
            • Standard Neck Dissection
            • Rome, Italy
              Fondazione Policlinico Universitario Agostino Gemelli IRCCS
            Mar 27, 2023

            Set for Head, Neck and Respiratory Disease in

            Completed
            • Mucopolysaccharidosis Type II
              • Manchester, Lancashire, United Kingdom
                Manchester University NHS Foundation Trust
              Aug 31, 2023

              Mucopolysaccharidosis Type II Natural History

              Completed
              • Mucopolysaccharidosis II
                • Pittsburgh, Pennsylvania
                • +2 more
                Apr 22, 2022

                Mucopolysaccharidosis II Trial in Netherlands, United States (DNL310)

                Recruiting
                • Mucopolysaccharidosis II
                • Oakland, California
                • +4 more
                Nov 14, 2022